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Patients voices: Rare diseases article
April 8, 2018 | Cushing's Disease: How an abortion pill turned out to be a treatment for a rare disease - The Washington Post article
Perth boy battling rare disease to run out with the Dockers article
A family's experience living with a rare disease article
Girl that suffers from Dock8 Immunodeficency syndrome who underwent a bone marrow transplant article
Gene therapy for thalassemia article
Life with Archer: Local family rallies around son with rare disease article
‘Super Sammy’ of Huber Heights Fighting Rare Heart Disorder article
Apraxia Awareness Day Sheds Light on New Disorder article
Can Surgery Cure Congenital Hyperinsulinism article
Windham girl fighting rare disease gets special honor article
Benefit for little girl with rare disease in Milladore article
Shooting hoops fundraiser held for 2 boys fighting rare disease article
Massimo Damiani's family determined to finish mission and find cure for rare disease leukodystrophy article
Rare in Common: Many Voices. One Mission. video
New Device Helps Patients with Addison's Disease Access Life-Saving Treatment article
Understanding ZSD webpage
Novel RNA-modifying tool corrects genetic diseases article
La Salle freshman lineman Gavin Robbins perseveres despite rare disease article
Siegel's Matt McCurry excels on baseball field after rare disease as infant article
Medical first: Twins treated for rare condition while still in the womb article
Who could resist the Happiest Walk in Canada? article
12-year-old educating medical students about rare disease article
CHMP adopts positive opinion for orphan drug to treat rare hereditary disease article
Topically-Applied Gene Tx Fast-Tracked for Dystrophic Epidermolysis Bullosa article
Rare disease patient graduates summa cum laude article
Five Things I've Learned About Living With a Rare Disease article
Girl with rare disease throws first pitch at Hagerstown Suns game article
Rare disorder can't keep indomitable Makenzie down for long article
Triathlete to bike through Utah while raising awareness for rare disease article
Why we walk: Ottawa residents say why they turn out for good causes article
She can't go out in the sun, but wanted to graduate with friends. This is how she did it article
Rare In Common: Hanging Out With Zebras: Life with a genetic mutation so rare it has never been reported before podcast
Tess Is Not Alone - A USP7 Story video
Osteogenesis Imperfecta National Conference webpage
New anti-ALS drug receives Orphan Drug designation (by EMA) article
Trial Results Are Positive For Two Rare Disease Gene Therapies article
Aberdeen student raising awareness of facial disfigurements article
New treatment approved for rare disease PKU article
Daughter with rare disorder inspires SJ native in race article
London-based hospital gives new lease of life to Bahraini girl suffering from rare condition article
Geoffrey Daintith hopes to walk again after being paralysed by Guillain-Barre syndrome article
Meet the boy with a rare skin condition that leaves his skin as fragile as a 'butterfly's wing' article
Six-month-old with rare condition fights through multiple surgeries article
Cross-Country Biker to Ride Through Utah While Raising Awareness for Rare Disease article
Experimental Treatment Offering Hope for Little Boy Diagnosed With Rare Disease article
Girl with rare disease plans more pool time this summer article
Local family raises thousands for children with rare disease article
Banking for the Future: How Biobanking Helps the Rare Disease Community article
Genetic "surgery" for rare diseases using Crispr article
Birth Triggered Rare, Deadly Illness in Mom Until Geneticist Solved the Mystery article
Churchland Sisters Have Broken Many Bones, But They Are By No Means Broken article
Rare Disease Causes 7-Year Old to Grow Older Before Her Time article
RARE Bears help comfort and connect kids with rare diseases article
Neenah Man to Walk 170 Miles in Ireland to Fight Rare Genetic Disease article
Dynacure secures $55 million Series A round for rare genetic disease treatment article
New Therapies on the Horizon for Huntington's Disease article
Indianapolis student awarded scholarship for accomplishments while living with rare genetic disease article
Banking for the Future: How Biobanking Helps the Rare Disease Community (Part 2 of 2) article
Alabama boy with rare disease will get "superpowers" during upcoming surgery article
Community rallies to help child with rare disease article
"Baby" King is not a baby anymore: Syracuse boy with rare disease ha outlived the odds article
Cleveland teen helps to research her own disease article
Teen Living With Rare Autoimmune Disease article
Huntington’s Disease: How Brain Training Games Could Help article
One of a Kind Kid article
If One Eye’s Brown and One Eye’s Blue, This Day is for You article
Family fighting against rare disease through annual fundraiser article
Baby battling rare disease arrives home after receiving potentially lifesaving treatment article