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Patients voices: Rare diseases
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April 8, 2018 | Cushing's Disease: How an abortion pill turned out to be a treatment for a rare disease - The Washington Post
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Perth boy battling rare disease to run out with the Dockers
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A family's experience living with a rare disease
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Girl that suffers from Dock8 Immunodeficency syndrome who underwent a bone marrow transplant
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Gene therapy for thalassemia
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Life with Archer: Local family rallies around son with rare disease
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‘Super Sammy’ of Huber Heights Fighting Rare Heart Disorder
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Apraxia Awareness Day Sheds Light on New Disorder
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Can Surgery Cure Congenital Hyperinsulinism
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Windham girl fighting rare disease gets special honor
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Benefit for little girl with rare disease in Milladore
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Shooting hoops fundraiser held for 2 boys fighting rare disease
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Massimo Damiani's family determined to finish mission and find cure for rare disease leukodystrophy
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Rare in Common: Many Voices. One Mission.
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New Device Helps Patients with Addison's Disease Access Life-Saving Treatment
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Understanding ZSD
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Novel RNA-modifying tool corrects genetic diseases
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La Salle freshman lineman Gavin Robbins perseveres despite rare disease
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Siegel's Matt McCurry excels on baseball field after rare disease as infant
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Medical first: Twins treated for rare condition while still in the womb
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Who could resist the Happiest Walk in Canada?
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12-year-old educating medical students about rare disease
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CHMP adopts positive opinion for orphan drug to treat rare hereditary disease
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Topically-Applied Gene Tx Fast-Tracked for Dystrophic Epidermolysis Bullosa
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Rare disease patient graduates summa cum laude
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Five Things I've Learned About Living With a Rare Disease
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Girl with rare disease throws first pitch at Hagerstown Suns game
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Rare disorder can't keep indomitable Makenzie down for long
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Triathlete to bike through Utah while raising awareness for rare disease
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Why we walk: Ottawa residents say why they turn out for good causes
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She can't go out in the sun, but wanted to graduate with friends. This is how she did it
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Rare In Common: Hanging Out With Zebras: Life with a genetic mutation so rare it has never been reported before
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Tess Is Not Alone - A USP7 Story
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Osteogenesis Imperfecta National Conference
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New anti-ALS drug receives Orphan Drug designation (by EMA)
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Trial Results Are Positive For Two Rare Disease Gene Therapies
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Aberdeen student raising awareness of facial disfigurements
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New treatment approved for rare disease PKU
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Daughter with rare disorder inspires SJ native in race
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London-based hospital gives new lease of life to Bahraini girl suffering from rare condition
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Geoffrey Daintith hopes to walk again after being paralysed by Guillain-Barre syndrome
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Meet the boy with a rare skin condition that leaves his skin as fragile as a 'butterfly's wing'
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Six-month-old with rare condition fights through multiple surgeries
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Cross-Country Biker to Ride Through Utah While Raising Awareness for Rare Disease
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Experimental Treatment Offering Hope for Little Boy Diagnosed With Rare Disease
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Girl with rare disease plans more pool time this summer
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Local family raises thousands for children with rare disease
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Banking for the Future: How Biobanking Helps the Rare Disease Community
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Genetic "surgery" for rare diseases using Crispr
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Birth Triggered Rare, Deadly Illness in Mom Until Geneticist Solved the Mystery
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Churchland Sisters Have Broken Many Bones, But They Are By No Means Broken
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Rare Disease Causes 7-Year Old to Grow Older Before Her Time
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RARE Bears help comfort and connect kids with rare diseases
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Neenah Man to Walk 170 Miles in Ireland to Fight Rare Genetic Disease
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Dynacure secures $55 million Series A round for rare genetic disease treatment
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New Therapies on the Horizon for Huntington's Disease
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Indianapolis student awarded scholarship for accomplishments while living with rare genetic disease
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Banking for the Future: How Biobanking Helps the Rare Disease Community (Part 2 of 2)
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Alabama boy with rare disease will get "superpowers" during upcoming surgery
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Community rallies to help child with rare disease
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"Baby" King is not a baby anymore: Syracuse boy with rare disease ha outlived the odds
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Cleveland teen helps to research her own disease
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Teen Living With Rare Autoimmune Disease
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Huntington’s Disease: How Brain Training Games Could Help
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One of a Kind Kid
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If One Eye’s Brown and One Eye’s Blue, This Day is for You
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Family fighting against rare disease through annual fundraiser
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Baby battling rare disease arrives home after receiving potentially lifesaving treatment
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